PharmD Info

A forum for Indian Pharmacy Professionals

Important: Registered today to have the complete access on this forum --- Register Here
Share any Pharmaceutical related news with appropriate reference. Latest Pharmaceutical News, Indian Pharma News,
  • User avatar
#2470
It’s a revolution when “US FDA” approved yesterday the FIRST gene-therapy medicine indicated for a disease other than cancer.

It’s “LUXTURNA” of “SPARK Therapeutics”.

There is a kind of vision-loss for people due to the defective gene namely “RPE65”.

“RPE65” gene produces a protein in our eye-cell which contributes to vision.

Vision-loss due to this “RPE65” gene is a hereditary disease and around 2000 people are being diagnosed in the USA every year.

“LUXTURNA” contains good “RPE65” genes and by administration of this to the eye can replace defective “RPE65” genes and thus can give vision.

Here, “trained”- virus carries the good “RPE65” genes to eyes.



Reference: https://www.fda.gov/NewsEvents/Newsroom ... 589467.htm

Tags

PharmD Info Online Group Discussion Disc[…]

The Pharmacy Council of India (PCI) has launched a[…]

Indian Association of Colleges of Pharmacy. A/C N[…]

PCI chalks out plans to allay concerns of educatio[…]

WELCOME TO OUR E-LEARN COURSE WORK MODULES